Table of Contents
Table of Contents 3
List of Tables 5
List of Figures 5
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Year, 2012 to YTD 2018 6
PTC Therapeutics Inc, Pharmaceuticals & Healthcare Deals By Type, 2012 to YTD 2018 7
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Region, 2012 to YTD 2018 8
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Therapy Area, 2012 to YTD 2018 9
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals Summary, 2012 to YTD 2018 10
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deal Details 12
Asset Purchase 12
PTC Therapeutics Acquires US Rights to Emflaza from Marathon Pharma 12
Venture Financing 14
Agilis Biotherapeutics Raises US$8 Million In Venture Financing 14
Agilis Biotherapeutics Raises USD8 Million in Venture Financing 15
PTC Therapeutics Raises USD4.5 Million in Financing 16
PTC Therapeutics Raises US$60 Million In Venture Financing 17
PTC Therapeutics Raises US$2 Million In Venture Financing 19
Ptc Therapeutics Raises US$30 Million In Venture Financing 20
Partnerships 22
PTC Therapeutics Enters into Agreement with CHDI Foundation 22
Agilis Biotherapeutics and Gene Therapy Research Institution Form Joint Venture 23
Agilis Biotherapeutics Partners with National Center for Accelerating Translational Sciences 24
Agilis Biotherapeutics Enters into Agreement with T-TOP Clinical Research 25
PTC Therapeutics Enters into Agreement with University of Pennsylvania 26
Pint Pharma Enter into Co-operation Agreement with PTC Therapeutics 27
Agilis Biotherapeutics Enters Into Co-Development Agreement With Intrexon 28
Licensing Agreements 29
PTC Therapeutics Enters into Licesing Agreement with Akcea Therapeutics 29
Agilis Biotherapeutics Enters into Licensing Agreement with National Taiwan University 30
PTC Therapeutics Enters into Licensing Agreement with Massachusetts General Hospital 31
Agilis Biotherapeutics Enters into Licensing Agreement with University of South Florida 32
Agilis Biotherapeutics Enters into Licensing Agreement with University of South Florida 33
Equity Offering 34
PTC Therapeutics Raises USD124.3 Million in Public Offering of Shares 34
Agilis Biotherapeutics Raises USD12.7 Million in Private Placement of Shares 36
PTC Therapeutics Raises USD125 Million in Public Offering of Shares 37
PTC Therapeutics Completes Public Offering Of Shares For US$126.5 Million 39
PTC Therapeutics Completes IPO For US$144.4 Million 41
PTC Therapeutics Raises USD53.9 Million in Private Placement of Preferred Shares 43
Debt Offering 44
PTC Therapeutics Raises USD150 Million in Private Placement of 3% Notes Due 2022 44
Acquisition 46
PTC Therapeutics Acquires Agilis Biotherapeutics 46
Sanofi May Acquire PTC Therapeutics 47
PTC Therapeutics Inc – Key Competitors 48
PTC Therapeutics Inc – Key Employees 49
PTC Therapeutics Inc – Locations And Subsidiaries 50
Head Office 50
Other Locations & Subsidiaries 50
Recent Developments 52
Financial Announcements 52
Nov 05, 2018: PTC Therapeutics reports third quarter 2018 financial results and provides a corporate update 52
Aug 07, 2018: PTC Therapeutics reports second quarter 2018 financial results and provides a corporate update 54
May 09, 2018: PTC Therapeutics Reports First Quarter 2018 Financial Results and Provides a Corporate Update 56
Mar 06, 2018: PTC Therapeutics Announces Fourth Quarter and Full Year 2017 Financial Results 58
Jan 08, 2018: PTC Therapeutics Provides Corporate Update and Outlines 2018 Strategic Priorities 60
Nov 02, 2017: PTC Therapeutics Reports Third Quarter 2017 Financial Results and Provides Corporate Update 61
Aug 08, 2017: PTC Therapeutics Reports Second Quarter 2017 Financial Results and Provides Corporate Update 63
May 08, 2017: PTC Therapeutics Reports First Quarter 2017 Financial Results and Provides Corporate Update 65
Mar 16, 2017: PTC Therapeutics Reports Fourth Quarter and Full Year 2016 Financial Results and Provides Corporate Update 66
Jan 09, 2017: PTC Therapeutics Provides Corporate Update and Outlines 2017 Strategic Priorities to Maximize the Global Value of Translarna and Advance its Innovative Pipeline 68
Corporate Communications 69
Jul 24, 2017: PTC Therapeutics Announces Promotion of Dr. Joseph McIntosh to Senior Vice President and Head of Clinical Development 69
Jun 05, 2017: PTC Therapeutics Announces Executive Promotions 70
Apr 10, 2017: PTC Therapeutics Announces Departure of Chief Financial Officer, Shane Kovacs 71
Government and Public Interest 72
Feb 13, 2018: PTC Therapeutics Launches Fourth Annual STRIVE Grant Award Program for Duchenne Muscular Dystrophy 72
Feb 08, 2017: PTC Therapeutics Announces Third Annual STRIVE Grant Award Program for Duchenne Muscular Dystrophy 73
Product News 74
05/14/2018: Agilis Biotherapeutics Announces Data Presentations on AADC Deficiency at the American Society of Gene and Cell Therapy 2018 Annual Meeting 74
05/11/2017: Agilis Biotherapeutics Announces Presentation of Five Year Follow-Up Data of Gene Therapy Treatment for AADC Deficiency 76
05/10/2017: Agilis Biotherapeutics Announces Presentation of Data from Phase I/II Trial for Treatment of AADC Deficiency 77
04/24/2018: Agilis Biotherapeutics Presents Platform Paper on AADC Deficiency Gene Therapy at American Academy of Neurology Annual Meeting 78
Product Approvals 79
Oct 31, 2017: Agilis Biotherapeutics Announces Orphan Product Designation Approval in Europe for the Treatment of Friedreich Ataxia 79
Feb 09, 2017: FDA Approves EMFLAZA (deflazacort) Tablets and Oral Suspension for the Treatment of Duchenne Muscular Dystrophy in Patients 5 Years and Older 80
Clinical Trials 81
Oct 03, 2017: Agilis Biotherapeutics Updates on Progress in CNS Gene Therapy Programs 81
Sep 06, 2017: Agilis Biotherapeutics Updates Progress of its CNS Gene Therapy for AADC Deficiency 83
Other Significant Developments 84
Jun 25, 2018: Decode Duchenne Announces 1,000th Patient Application 84
Appendix 85
Methodology 85
About GlobalData 85
Contact Us 85
Disclaimer 85
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Key Facts, 2017 2
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Year, 2012 to YTD 2018 6
PTC Therapeutics Inc, Pharmaceuticals & Healthcare Deals By Type, 2012 to YTD 2018 7
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Region, 2012 to YTD 2018 8
PTC Therapeutics Inc, Deals By Therapy Area, 2012 to YTD 2018 9
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals Summary, 2012 to YTD 2018 10
PTC Therapeutics Acquires US Rights to Emflaza from Marathon Pharma 12
Agilis Biotherapeutics Raises US$8 Million In Venture Financing 14
Agilis Biotherapeutics Raises USD8 Million in Venture Financing 15
PTC Therapeutics Raises USD4.5 Million in Financing 16
PTC Therapeutics Raises US$60 Million In Venture Financing 17
PTC Therapeutics Raises US$2 Million In Venture Financing 19
Ptc Therapeutics Raises US$30 Million In Venture Financing 20
PTC Therapeutics Enters into Agreement with CHDI Foundation 22
Agilis Biotherapeutics and Gene Therapy Research Institution Form Joint Venture 23
Agilis Biotherapeutics Partners with National Center for Accelerating Translational Sciences 24
Agilis Biotherapeutics Enters into Agreement with T-TOP Clinical Research 25
PTC Therapeutics Enters into Agreement with University of Pennsylvania 26
Pint Pharma Enter into Co-operation Agreement with PTC Therapeutics 27
Agilis Biotherapeutics Enters Into Co-Development Agreement With Intrexon 28
PTC Therapeutics Enters into Licesing Agreement with Akcea Therapeutics 29
Agilis Biotherapeutics Enters into Licensing Agreement with National Taiwan University 30
PTC Therapeutics Enters into Licensing Agreement with Massachusetts General Hospital 31
Agilis Biotherapeutics Enters into Licensing Agreement with University of South Florida 32
Agilis Biotherapeutics Enters into Licensing Agreement with University of South Florida 33
PTC Therapeutics Raises USD124.3 Million in Public Offering of Shares 34
Agilis Biotherapeutics Raises USD12.7 Million in Private Placement of Shares 36
PTC Therapeutics Raises USD125 Million in Public Offering of Shares 37
PTC Therapeutics Completes Public Offering Of Shares For US$126.5 Million 39
PTC Therapeutics Completes IPO For US$144.4 Million 41
PTC Therapeutics Raises USD53.9 Million in Private Placement of Preferred Shares 43
PTC Therapeutics Raises USD150 Million in Private Placement of 3% Notes Due 2022 44
PTC Therapeutics Acquires Agilis Biotherapeutics 46
Sanofi May Acquire PTC Therapeutics 47
PTC Therapeutics Inc, Key Competitors 48
PTC Therapeutics Inc, Key Employees 49
PTC Therapeutics Inc, Other Locations 50
PTC Therapeutics Inc, Subsidiaries 50
List of Figures
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals by Type, 2012 to YTD 2018 2
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Year, 2012 to YTD 2018 2
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Region, 2012 to YTD 2018 2
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Therapy Area, 2012 to YTD 2018 2
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Year, 2012 to YTD 2018 6
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals by Type, 2012 to YTD 2018 7
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Region, 2012 to YTD 2018 8
PTC Therapeutics Inc, Pharmaceuticals & Healthcare, Deals By Therapy Area, 2012 to YTD 2018 9